Viewing Study NCT04105166


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Study NCT ID: NCT04105166
Status: COMPLETED
Last Update Posted: 2025-09-05
First Post: 2019-09-24
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Gene Therapy for Pyruvate Kinase Deficiency (PKD)
Sponsor: Rocket Pharmaceuticals Inc.
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Pyruvate Kinase Deficiency View
Keywords:

Keywords

Keyword Brief Keyword Text View
None hemolytic anemia View
None anemia View
None gene therapy View