Viewing Study NCT03694561


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Study NCT ID: NCT03694561
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-09-22
First Post: 2018-10-01
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Developing a Management Approach for Patients With "Late-Onset" Pompe Disease
Sponsor: Duke University
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Pompe Disease View
None Pompe Disease (Late-onset) View
None GAA Deficiency View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Pompe disease View
None Glycogen Storage Disease Type II View
None Acid Maltase Deficiency View
None Acid Alpha-Glucosidase Deficiency View
None Alglucosidase alfa View
None Newborn Screening View