Viewing StudyNCT03478670



Ignite Creation Date: 2024-05-06 @ 11:15 AM
Last Modification Date: 2024-10-26 @ 12:43 PM
Study NCT ID: NCT03478670
Status: ENROLLING_BY_INVITATION
Last Update Posted: 2024-01-29
First Post: 2018-03-23

Brief Title: Strimvelis Registry Study to Follow-up Patients With Adenosine Deaminase Severe Combined Immunodeficiency ADA-SCID
Sponsor: Fondazione Telethon
Organization: Fondazione Telethon

Conditions & Keywords Data

Conditions:
Name
Immunologic Deficiency Syndromes
Keywords:
Name View
Strimvelis View
gene therapy View
retroviral vector View
inherited immune disorder View
ADA-SCID View
previously GSK2696273 View