Viewing StudyNCT03432364



Ignite Creation Date: 2024-05-06 @ 11:07 AM
Last Modification Date: 2024-10-26 @ 12:40 PM
Study NCT ID: NCT03432364
Status: COMPLETED
Last Update Posted: 2023-12-14
First Post: 2018-02-01

Brief Title: A Study to Assess the Safety Tolerability and Efficacy of ST-400 for Treatment of Transfusion-Dependent Beta-thalassemia TDT
Sponsor: Sangamo Therapeutics
Organization: Sangamo Therapeutics

Conditions & Keywords Data

Conditions:
Name
Transfusion Dependent Beta-thalassemia
Keywords:
Name View
zinc finger nuclease View
Beta thalassemia View
Beta-thalassemia View
Thalassemia major View
Cooleys anemia View
ZFN mediated genome editing View