Viewing StudyNCT03381729



Ignite Creation Date: 2024-05-06 @ 10:56 AM
Last Modification Date: 2024-10-26 @ 12:37 PM
Study NCT ID: NCT03381729
Status: TERMINATED
Last Update Posted: 2023-04-24
First Post: 2017-12-13

Brief Title: Study of Intrathecal Administration of Onasemnogene Abeparvovec-xioi for Spinal Muscular Atrophy
Sponsor: Novartis Gene Therapies
Organization: Novartis

Conditions & Keywords Data

Conditions:
Name
Spinal Muscular Atrophy
Keywords:
Name View
AAV9 View
Gene Transfer View
Gene Therapy View
Adeno-associated virus View
Survival Motor Neuron View
SMN View