Viewing Study NCT03564561

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Ignite Creation Date: 2025-12-24 @ 12:21 PM
Ignite Modification Date: 2026-01-24 @ 9:56 PM
Study NCT ID: NCT03564561
Status: RECRUITING
Last Update Posted: 2024-04-08
First Post: 2018-03-27
Is NOT Gene Therapy: True
Has Adverse Events: False
Brief Title: Natural History of Pompe Disease
Sponsor: Assistance Publique - Hôpitaux de Paris
Organization:
Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Glycogen Storage Disease Type II, Adult View
Keywords:

Keywords

Keyword Brief Keyword Text View
None glycogen storage disease type II, adult View
None Pompe disease View
None clinical evolution View
None molecular evolution View
None follow-up View
None c.-32-13T>G mutation View
None antisense oligonucleotide treatment View
None in vitro View