Viewing Study NCT04768166


Ignite Creation Date: 2025-12-24 @ 4:19 PM
Ignite Modification Date: 2026-02-01 @ 10:02 PM
Study NCT ID: NCT04768166
Status: COMPLETED
Last Update Posted: 2022-04-11
First Post: 2021-02-12
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Testing Miglustat Administration in Subjects With Spastic Paraplegia 11
Sponsor: IRCCS Fondazione Stella Maris
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Hereditary Spastic Paraparesis View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Autophagic Lysosome Reformation View
None SPG11 View
None Miglustat View
None Lisosomal Storage Disorders View