Ignite Creation Date:
2025-12-24 @ 4:13 PM
Ignite Modification Date:
2026-02-04 @ 11:07 PM
Study NCT ID:
NCT07125066
Status:
ENROLLING_BY_INVITATION
Last Update Posted:
2025-08-15
First Post:
2025-07-30
Is NOT Gene Therapy:
True
Has Adverse Events:
False
Brief Title:
An Individual Patient, Open Label Study to Use ACER-001 to Treat Combined D,L-2 Hydroxyglutaric Aciduria (C-2HGA)
Sponsor:
Jerry Vockley, MD, PhD
Organization: