Viewing Study NCT00410566


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Study NCT ID: NCT00410566
Status: TERMINATED
Last Update Posted: 2015-03-19
First Post: 2006-12-11
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Safety Study of rhASM Enzyme Replacement Therapy in Adults With Acid Sphingomyelinase Deficiency (Niemann-Pick Disease)
Sponsor: Genzyme, a Sanofi Company
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Acid Sphingomyelinase Deficiency View
None Niemann-Pick Disease View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Acid sphingomyelinase deficiency View
None Niemann-Pick disease View
None Lysosomal storage disorder View
None Enzyme replacement therapy View
None Treatment View