Viewing StudyNCT02725580



Ignite Creation Date: 2024-05-06 @ 8:22 AM
Last Modification Date: 2024-10-26 @ 11:59 AM
Study NCT ID: NCT02725580
Status: COMPLETED
Last Update Posted: 2023-03-08
First Post: 2016-03-16

Brief Title: Gene Therapy For Children With Variant Late Infantile Neuronal Ceroid Lipofuscinosis 6 vLINCL6 Disease
Sponsor: Amicus Therapeutics
Organization: Amicus Therapeutics

Conditions & Keywords Data

Conditions:
Name
Variant Late-Infantile Neuronal Ceroid Lipofuscinosis
Keywords:
Name View
Batten Disease View
Neuronal ceroid lipofuscinosis NCL View
CLN6 View
vLINCL6 View
Gene Transfer View
CLN6 Batten Disease View