Viewing StudyNCT02534844



Ignite Creation Date: 2024-05-06 @ 7:25 AM
Last Modification Date: 2024-10-26 @ 11:48 AM
Study NCT ID: NCT02534844
Status: COMPLETED
Last Update Posted: 2023-02-22
First Post: 2015-08-18

Brief Title: VTS-270 to Treat Niemann-Pick Type C1 NPC1 Disease
Sponsor: Mandos LLC
Organization: Mandos LLC

Conditions & Keywords Data

Conditions:
Name
Niemann-Pick Disease Type C
Keywords:
Name View
pediatrics View
Niemann-Pick Type C1 NPC1 Disease View
neurologic disease View
gross motor dysfunction View
fine motor dysfunction View
dysphagia View
swallowing problems View
cognitive dysfunction View
gait abnormalities View