Viewing StudyNCT02214160



Ignite Creation Date: 2024-05-06 @ 3:08 AM
Last Modification Date: 2024-10-26 @ 11:29 AM
Study NCT ID: NCT02214160
Status: COMPLETED
Last Update Posted: 2023-08-01
First Post: 2014-08-06

Brief Title: Long-Chain Fatty Acid Oxidation Disorders LC-FAOD Extension Study for Subjects Previously Enrolled in Triheptanoin Studies
Sponsor: Ultragenyx Pharmaceutical Inc
Organization: Ultragenyx Pharmaceutical Inc

Conditions & Keywords Data

Conditions:
Name
Carnitine-acylcarnitine Translocase CACT Deficiency
Carnitine Palmitoyltransferase CPT I or CPT II Deficiency
Very Long Chain Acyl-CoA Dehydrogenase VLCAD Deficiency
Long-chain 3-hydroxy-acyl-CoA Dehydrogenase LCHAD Deficiency
Trifunctional Protein TFP Deficiency
Keywords:
Name View
C7 View
Long-Chain Fatty Acid Oxidation Disorders LC-FAOD View
carnitine palmitoyltransferase CPT I or CPT II deficiency View
very long chain acyl-CoA dehydrogenase VLCAD deficiency View
long-chain 3-hydroxy-acyl-CoA dehydrogenase LCHAD deficiency View
trifunctional protein TFP deficiency View
carnitine-acylcarnitine translocase CACT deficiency View
Triheptanoin View
UX007 View