Viewing Study NCT02090959


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Study NCT ID: NCT02090959
Status: TERMINATED
Last Update Posted: 2020-08-11
First Post: 2014-03-17
Is Gene Therapy: True
Has Adverse Events: True

Brief Title: An Extension Study of Ataluren (PTC124) in Participants With Nonsense Mutation Dystrophinopathy
Sponsor: PTC Therapeutics
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Muscular Dystrophy, Duchenne View
None Muscular Dystrophies View
None Muscular Disorders, Atrophic View
None Muscular Diseases View
None Musculoskeletal Diseases View
None Neuromuscular Diseases View
None Nervous System Diseases View
None Genetic Diseases, X-Linked View
None Genetic Diseases, Inborn View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Duchenne muscular dystrophy View
None Dystrophinopathy View
None Nonsense mutation View
None Premature stop codon View
None Becker muscular dystrophy View
None DMD/BMD View
None PTC124 View
None Ataluren View