Viewing StudyNCT02122952



Ignite Creation Date: 2024-05-06 @ 2:47 AM
Last Modification Date: 2024-10-26 @ 11:23 AM
Study NCT ID: NCT02122952
Status: COMPLETED
Last Update Posted: 2022-09-15
First Post: 2014-04-23

Brief Title: Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1
Sponsor: Novartis Gene Therapies
Organization: Novartis

Conditions & Keywords Data

Conditions:
Name
Spinal Muscular Atrophy 1
Keywords:
Name View
AAV9 View
Gene Transfer View
Gene Therapy View
Adeno-associated virus View
Survival Motor Neuron View
SMN View