Ignite Creation Date:
2025-12-24 @ 12:07 PM
Ignite Modification Date:
2026-02-25 @ 7:23 PM
Study NCT ID:
NCT02047461
Status:
COMPLETED
Last Update Posted:
2023-10-17
First Post:
2014-01-09
Is Gene Therapy:
True
Has Adverse Events:
True
Brief Title:
Safety & Efficacy Study of ORGN001 (Formerly ALXN1101) in Pediatric Patients With MoCD Type A Currently Treated With rcPMP
Sponsor:
Origin Biosciences
Organization:
Conditions & Keywords Data
Conditions:
Conditions
| Condition Brief | Condition Text | View |
|---|---|---|
| None | Molybdenum Cofactor Deficiency, Type A | View |