Viewing StudyNCT02022696



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Last Modification Date: 2024-10-26 @ 11:17 AM
Study NCT ID: NCT02022696
Status: COMPLETED
Last Update Posted: 2017-09-27
First Post: 2013-12-20

Brief Title: Treatment of SCID Due to ADA Deficiency With Autologous Transplantation of Cord Blood or Hematopoietic CD 34 Cells After Addition of a Normal Human ADA cDNA by the EFS-ADA Lentiviral Vector
Sponsor: National Human Genome Research Institute NHGRI
Organization: National Institutes of Health Clinical Center CC

Conditions & Keywords Data

Conditions:
Name
ADA-SCID
Adenosine Deaminase Deficiency
Keywords:
Name View
Lentiviral Vectors View
Adenosine Deaminase Deficiency View
Gene Therapy View