Viewing Study NCT06455059


Ignite Creation Date: 2025-12-24 @ 2:58 PM
Ignite Modification Date: 2026-02-06 @ 4:24 PM
Study NCT ID: NCT06455059
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-10-14
First Post: 2024-06-07
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Interventional Study of Vosoritide for the Treatment of Children With Hypochondroplasia
Sponsor: BioMarin Pharmaceutical
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Hypochondroplasia View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Hypochondroplasia View
None Dwarfism View
None Bone Diseases View
None Bone Disease, Developmental View
None HCH View
None Natriuretic Peptide, C-Type View
None Musculoskeletal Diseases View
None Natriuretic Agents View
None Physiological Effects of Drugs View
None Skeletal Dysplasias View
None Genetic Diseases, Inborn View
None Osteochondrodysplasias View
None Vosoritide View
None Voxzogo View