Viewing StudyNCT01886378



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Last Modification Date: 2024-10-26 @ 11:09 AM
Study NCT ID: NCT01886378
Status: COMPLETED
Last Update Posted: 2021-02-11
First Post: 2013-06-18

Brief Title: A Study of UX007 Triheptanoin in Participants With Long-Chain Fatty Acid Oxidation Disorders LC-FAOD
Sponsor: Ultragenyx Pharmaceutical Inc
Organization: Ultragenyx Pharmaceutical Inc

Conditions & Keywords Data

Conditions:
Name
Trifunctional Protein TFP Deficiency
Long-chain Fatty Acid Oxidation Disorders LC-FAOD
Carnitine Palmitoyltransferase CPT II Deficiency
Very Long Chain Acyl-CoA Dehydrogenase VLCAD Deficiency
Longchain 3-hydroxy-acyl-CoA Dehydrogenase LCHAD Deficiency
Keywords:
Name View
C7 View
FAOD View
VLCAD View
CPT II View
CPT2 View
CPT 2 View
LCHAD View
UX007 View
Triheptanoin View
TFP View