Viewing StudyNCT01852071



Ignite Creation Date: 2024-05-06 @ 1:37 AM
Last Modification Date: 2024-10-26 @ 11:06 AM
Study NCT ID: NCT01852071
Status: COMPLETED
Last Update Posted: 2022-08-03
First Post: 2013-05-07

Brief Title: Autologous CD34 Hematopoietic Stem Cells Transduced ex Vivo With Elongation Factor 1 Alpha Shortened EFS Lentiviral Vector Encoding for the Human ADA Gene
Sponsor: University of California Los Angeles
Organization: University of California Los Angeles

Conditions & Keywords Data

Conditions:
Name
ADA-SCID
Keywords:
Name View
lentiviral vector View
gene therapy View
hematopoietic stem cell View
ADA-SCID View