Ignite Creation Date:
2025-12-25 @ 4:58 AM
Ignite Modification Date:
2026-03-04 @ 3:44 PM
Study NCT ID:
NCT04201418
Status:
COMPLETED
Last Update Posted:
2022-06-06
First Post:
2019-12-13
Is NOT Gene Therapy:
True
Has Adverse Events:
False
Brief Title:
A Multicenter Observational Study to Evaluate the Effectiveness of Patisiran in Patients With Polyneuropathy of ATTRv Amyloidosis With a V122I or T60A Mutation
Sponsor:
Alnylam Pharmaceuticals
Organization:
Conditions & Keywords Data
Conditions:
Keywords:
Keywords
| Keyword Brief | Keyword Text | View |
|---|---|---|
| None | Valine to isoleucine substitution at position 122 | View |
| None | V122I | View |
| None | Threonine to alanine substitution at position 60 | View |
| None | T60A | View |
| None | Familial Amyloid Polyneuropathies | View |
| None | ATTR | View |
| None | Transthyretin amyloidosis | View |
| None | Transthyretin | View |
| None | Amyloidosis | View |
| None | TTR-mediated Amyloidosis | View |
| None | RNAi therapeutic | View |
| None | FAP | View |
| None | Polyneuropathies | View |
| None | Amyloid neuropathies | View |
| None | Amyloid neuropathies, familial | View |
| None | Amyloidosis, familial | View |
| None | Peripheral nervous system diseases | View |
| None | Nervous system diseases | View |
| None | TTR | View |
| None | Neuromuscular diseases | View |
| None | Proteostasis deficiencies | View |
| None | Metabolic diseases | View |
| None | Heredodegenerative disorders, nervous system | View |
| None | Neurodegenerative diseases | View |
| None | Genetic diseases, inborn | View |
| None | Metabolism, inborn errors | View |
| None | ATTRv | View |