Viewing Study NCT02057718


Ignite Creation Date: 2025-12-25 @ 4:35 AM
Ignite Modification Date: 2026-03-05 @ 10:15 PM
Study NCT ID: NCT02057718
Status: COMPLETED
Last Update Posted: 2023-10-23
First Post: 2014-02-05
Is NOT Gene Therapy: True
Has Adverse Events: True

Brief Title: Open Label Study to Evaluate Efficacy and Long Term Safety of LUM001 (Maralixibat) in the Treatment of Cholestatic Liver Disease in Patients With Progressive Familial Intrahepatic Cholestasis
Sponsor: Mirum Pharmaceuticals, Inc.
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Progressive Familial Intrahepatic Cholestasis (PFIC) View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Bile duct diseases View
None Intrahepatic Cholestasis View
None Cholestasis View
None PFIC View
None Pruritus View
None Cholestatic Liver Disease View