Viewing Study NCT03602820


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Ignite Modification Date: 2025-12-26 @ 3:31 AM
Study NCT ID: NCT03602820
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-04-18
First Post: 2018-07-18
Is NOT Gene Therapy: False
Has Adverse Events: False

Brief Title: Long-term Follow-up Study in Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2)
Sponsor: Spark Therapeutics, Inc.
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Inherited Retinal Dystrophy Due to RPE65 Mutations View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Leber congenital amaurosis, retinitis pigmentosa View