Viewing Study NCT00007020


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Study NCT ID: NCT00007020
Status: COMPLETED
Last Update Posted: 2023-10-03
First Post: 2000-12-06
Is NOT Gene Therapy: True
Has Adverse Events: True

Brief Title: Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid
Sponsor: Mirum Pharmaceuticals, Inc.
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Infantile Refsum's Disease View
None Zellweger Syndrome View
None Adrenoleukodystrophy View
None Peroxisomal Disorders View
None Cholestasis View
Keywords: