Viewing Study NCT07014020

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Ignite Creation Date: 2025-12-25 @ 4:17 AM
Ignite Modification Date: 2026-03-27 @ 1:36 AM
Study NCT ID: NCT07014020
Status: RECRUITING
Last Update Posted: 2025-07-30
First Post: 2025-05-21
Is Gene Therapy: True
Has Adverse Events: False
Brief Title: RB001 Gene Therapy Study in Children With SHANK3-related Phelan McDermid Syndrome (PMS)
Sponsor: Peking University First Hospital
Organization:
Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Phelan-McDermid Syndrome View
None SHANK3 Haploinsufficiency View
Keywords:

Keywords

Keyword Brief Keyword Text View
None AAV View
None SHANK3 View
None Phelan-Mecdermid Syndrome View
None 22q13.3 deletion syndrome View