Viewing Study NCT05898620


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Ignite Modification Date: 2026-01-29 @ 6:59 PM
Study NCT ID: NCT05898620
Status: RECRUITING
Last Update Posted: 2025-12-17
First Post: 2023-06-01
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett Syndrome
Sponsor: Neurogene Inc.
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Rett Syndrome View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Typical Rett Syndrome View
None MECP2 View
None Rett Disorder View
None Genetic Diseases, Inborn View
None Genetic Diseases, X-Linked View
None Neurodevelopmental Disorders View
None Neurobehavioral Manifestations View
None Neurologic Manifestations View
None Intellectual Disability View
None Nervous System Diseases View
None Pathologic Processes View
None RTT View