Viewing StudyNCT01697319



Ignite Creation Date: 2024-05-06 @ 12:57 AM
Last Modification Date: 2024-10-26 @ 10:57 AM
Study NCT ID: NCT01697319
Status: TERMINATED
Last Update Posted: 2016-01-12
First Post: 2012-09-17

Brief Title: Efficacy and Safety Study of BMN 110 for Morquio A Syndrome Patients Who Have Limited Ambulation
Sponsor: BioMarin Pharmaceutical
Organization: BioMarin Pharmaceutical

Conditions & Keywords Data

Conditions:
Name
MPS IVA
Mucopolysaccharidosis IVA
Morquio A Syndrome
Keywords:
Name View
Grip Pinch View
Mucopolysaccharidosis IVA Type A View
MPS IVA Type A View
Mucopolysaccharidosis IVA View
MPS IVA View
Morquio A Syndrome View
Lysosomal Storage Disorder View
LSD View
N-acetylgalactosamine-6-sulfatase View
N-acetylgalactosamine-6-sulfate View
sulfatase View
galactose-6-sulfatase View
GALNS View
enzyme replacement therapy View
ERT View
MOR-006 View
CPET View
Limited ambulation View