Viewing StudyNCT01609062



Ignite Creation Date: 2024-05-06 @ 12:33 AM
Last Modification Date: 2024-10-26 @ 10:52 AM
Study NCT ID: NCT01609062
Status: TERMINATED
Last Update Posted: 2016-02-01
First Post: 2012-05-24

Brief Title: Safety and Exercise Study of Two Doses of BMN 110 for Morquio A Syndrome
Sponsor: BioMarin Pharmaceutical
Organization: BioMarin Pharmaceutical

Conditions & Keywords Data

Conditions:
Name
MPS IVA
Mucopolysaccharidosis IVA
Morquio A Syndrome
Keywords:
Name View
Mucopolysaccharidosis IVA Type A View
MPS IVA Type A View
Mucopolysaccharidosis IVA View
MPS IVA View
Morquio A Syndrome View
Lysosomal Storage Disorder View
LSD View
N-acetylgalactosamine-6-sulfatase View
N-acetylgalactosamine-6-sulfate View
sulfatase View
galactose-6-sulfatase View
GALNS View
enzyme replacement therapy View
ERT View
MOR-008 View
CPET View
MST View
muscle strength test View
physiological effect View