Ignite Creation Date:
2025-12-25 @ 3:20 AM
Ignite Modification Date:
2026-02-25 @ 5:51 PM
Study NCT ID:
NCT04126005
Status:
ACTIVE_NOT_RECRUITING
Last Update Posted:
2025-06-22
First Post:
2019-10-10
Is NOT Gene Therapy:
True
Has Adverse Events:
False
Brief Title:
Natural History Study of Patients With Canavan Disease (CANinform Study)
Sponsor:
Aspa Therapeutics
Organization:
Conditions & Keywords Data
Conditions:
Conditions
| Condition Brief | Condition Text | View |
|---|---|---|
| None | Canavan Disease | View |
Keywords:
Keywords
| Keyword Brief | Keyword Text | View |
|---|---|---|
| None | Canavan Disease | View |
| None | AAV | View |
| None | AAV9 | View |
| None | Gene therapy | View |
| None | Aspartoacylase | View |
| None | ASPA | View |
| None | ASPA gene | View |
| None | rAAV9 | View |
| None | ACY2 | View |
| None | Aminoacylase 2 | View |
| None | Spongy degeneration | View |
| None | N-acetyl-L-aspartic acid (NAA) | View |
| None | N-acetylaspartate | View |
| None | Rare disease | View |
| None | Inherited Metabolic Disorders | View |
| None | Leukodystrophy | View |
| None | Leukoencephalopathies | View |
| None | Autosomal Recessive Disorder | View |
| None | Neurodevelopmental diseases | View |
| None | CANinform Study | View |