Viewing Study NCT03003533


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Study NCT ID: NCT03003533
Status: COMPLETED
Last Update Posted: 2024-12-30
First Post: 2016-12-16
Is NOT Gene Therapy: True
Has Adverse Events: True

Brief Title: A Gene Transfer Study for Hemophilia A
Sponsor: Spark Therapeutics, Inc.
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Hemophilia A View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Adeno-Associated Virus (AAV) View
None Blood Coagulation Disorders View
None Blood Coagulation Disorders, Inherited View
None Coagulation Protein Disorders View
None Factor VIII (FVIII) View
None Factor VIII (FVIII) Deficiency View
None Factor VIII (FVIII) Gene View
None Factor VIII (FVIII) Protein View
None Genetic Diseases, Inborn View
None Genetic Diseases, X-Linked View
None Gene Therapy View
None Gene Transfer View
None Hematologic Diseases View
None Hemorrhagic Disorders View
None Recombinant View
None Vector View