Viewing StudyNCT01515956



Ignite Creation Date: 2024-05-06 @ 12:11 AM
Last Modification Date: 2024-10-26 @ 10:46 AM
Study NCT ID: NCT01515956
Status: COMPLETED
Last Update Posted: 2017-08-10
First Post: 2011-12-22

Brief Title: Study of BMN 110 in Pediatric Patients 5 Years of Age With Mucopolysaccharidosis IVA Morquio A Syndrome
Sponsor: BioMarin Pharmaceutical
Organization: BioMarin Pharmaceutical

Conditions & Keywords Data

Conditions:
Name
MPS IVA
Mucopolysaccharidosis IVA
Morquio A Syndrome
Keywords:
Name View
ERT View
Mucopolysaccharidosis IVA type A View
MPS IVA Type A View
Mucopolysaccharidosis IVA View
MPS IVA View
Morquio A Syndrome View
Lysosomal Storage Disorder View
LSD View
N-acetylgalactosamine-6-sulfatase View
N-acetylgalactosamine-6-sulfate View
sulfatase View
galactose-6-sulfatase View
GALNS View
enzyme replacement therapy View