Ignite Creation Date:
2024-05-05 @ 11:59 PM
Last Modification Date:
2024-10-26 @ 10:42 AM
Study NCT ID:
NCT01461304
Status:
NO_LONGER_AVAILABLE
Last Update Posted:
2021-12-10
First Post:
2011-10-25
Brief Title:
Compassionate Use of Triheptanoin C7 for Inherited Disorders of Energy Metabolism
Sponsor:
Jerry Vockley MD PhD
Organization:
University of Pittsburgh
Conditions & Keywords Data
Conditions:
| Name |
|---|
| Barth Syndrome |
| Very Long-chain acylCoA Dehydrogenase VLCAD Deficiency |
| Carnitine Palmitoyltransferase Deficiencies CPT1 CPT2 |
| Mitochondrial Trifunctional Protein Deficiency |
| Long-chain Hydroxyacyl-CoA Dehydrogenase Deficiency |
| Glycogen Storage Disorders |
| Pyruvate Carboxylase Deficiency Disease |
| ACYL-CoA DEHYDROGENASE FAMILY MEMBER 9 DEFICIENCY of |