Viewing Study NCT04088734


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Ignite Modification Date: 2026-03-06 @ 11:46 PM
Study NCT ID: NCT04088734
Status: TERMINATED
Last Update Posted: 2023-07-25
First Post: 2019-09-11
Is Gene Therapy: True
Has Adverse Events: True

Brief Title: Gene Transfer Study of ABO-102 in Patients With Middle and Advanced Phases of MPS IIIA Disease
Sponsor: Ultragenyx Pharmaceutical Inc
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None MPS IIIA View
None Sanfilippo Syndrome View
None Sanfilippo A View
None Mucopolysaccharidosis III View
Keywords:

Keywords

Keyword Brief Keyword Text View
None MPS IIIA View
None Sanfilippo View
None Gene therapy View