Viewing Study NCT06363760


Ignite Creation Date: 2025-12-25 @ 2:17 AM
Ignite Modification Date: 2026-02-23 @ 8:07 PM
Study NCT ID: NCT06363760
Status: ENROLLING_BY_INVITATION
Last Update Posted: 2025-04-02
First Post: 2024-04-09
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: A Long-Term Follow-Up Study of Participants With Sickle Cell Disease or Transfusion Dependent β-Thalassemia Who Received EDIT-301
Sponsor: Editas Medicine, Inc.
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Sickle Cell Disease View
None Transfusion-dependent Beta-Thalassemia View
None Hemoglobinopathies View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Sickle Cell Disease View
None Sickle Cell Anemia View
None Sickling Disorder Due to Hemoglobin S View
None Beta-Thalassemia View
None Thalassemia Major View
None Thalassemia Intermedia View
None Hemoglobinopathies View
None CRISPR-Cas12a View
None Autologous CD34+ View
None Genetic Diseases, Inborn View
None Hematologic Diseases View
None Anemia View
None Anemia, Hemolytic, Congenital View
None Anemia, Hemolytic View