Ignite Creation Date:
2025-12-25 @ 2:10 AM
Ignite Modification Date:
2026-02-25 @ 10:04 PM
Study NCT ID:
NCT02214160
Status:
COMPLETED
Last Update Posted:
2023-08-01
First Post:
2014-08-06
Is NOT Gene Therapy:
True
Has Adverse Events:
True
Brief Title:
Long-Chain Fatty Acid Oxidation Disorders (LC-FAOD) Extension Study for Subjects Previously Enrolled in Triheptanoin Studies
Sponsor:
Ultragenyx Pharmaceutical Inc
Organization:
Conditions & Keywords Data
Conditions:
Conditions
| Condition Brief | Condition Text | View |
|---|---|---|
| None | Carnitine Palmitoyltransferase (CPT I or CPT II) Deficiency | View |
| None | Very Long Chain Acyl-CoA Dehydrogenase (VLCAD) Deficiency | View |
| None | Long-chain 3-hydroxy-acyl-CoA Dehydrogenase (LCHAD) Deficiency | View |
| None | Trifunctional Protein (TFP) Deficiency | View |
| None | Carnitine-acylcarnitine Translocase (CACT) Deficiency | View |
Keywords:
Keywords
| Keyword Brief | Keyword Text | View |
|---|---|---|
| None | Long-Chain Fatty Acid Oxidation Disorders (LC-FAOD) | View |
| None | carnitine palmitoyltransferase (CPT I or CPT II) deficiency | View |
| None | very long chain acyl-CoA dehydrogenase (VLCAD) deficiency | View |
| None | long-chain 3-hydroxy-acyl-CoA dehydrogenase (LCHAD) deficiency | View |
| None | trifunctional protein (TFP) deficiency | View |
| None | carnitine-acylcarnitine translocase (CACT) deficiency | View |
| None | Triheptanoin | View |
| None | UX007 | View |
| None | C7 | View |