Ignite Creation Date:
2025-12-25 @ 2:10 AM
Ignite Modification Date:
2026-02-19 @ 1:26 PM
Study NCT ID:
NCT04049760
Status:
COMPLETED
Last Update Posted:
2025-06-17
First Post:
2019-07-30
Is Gene Therapy:
True
Has Adverse Events:
True
Brief Title:
Safety, Pharmacodynamics, and Efficacy of Migalastat in Pediatric Subjects (Aged >12 Years) With Fabry Disease
Sponsor:
Amicus Therapeutics
Organization: