Viewing Study NCT04925960


Ignite Creation Date: 2025-12-25 @ 2:10 AM
Ignite Modification Date: 2026-01-06 @ 6:21 PM
Study NCT ID: NCT04925960
Status: TERMINATED
Last Update Posted: 2025-09-25
First Post: 2021-06-08
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Oral Epalrestat Therapy in Pediatric Subjects With PMM2-CDG
Sponsor: Maggie's Pearl, LLC
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Pmm2-CDG View
None Phosphomannomutase 2 Deficiency View
None Phosphomannomutase 2 Congenital Disorder of Glycosylation View
None Phosphomannomutase II Congenital Disorder of Glycosylation View
None Phosphomannomutase II Deficiency View
Keywords: