Viewing Study NCT04576494


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Study NCT ID: NCT04576494
Status: COMPLETED
Last Update Posted: 2024-12-04
First Post: 2020-09-29
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Study of the Functional Effects of Nusinersen in 5q-spinal Muscular Amyotrophy Adults (SMA Type 2 or 3 Forms)
Sponsor: CHU de Reims
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Spinal Muscular Atrophy View
Keywords:

Keywords

Keyword Brief Keyword Text View
None oligonucleotides View
None survival of motor 2 protein View
None muscular atrophy View
None quality of life View
None genetic therapy View
None single-case studies as topic View
None humans View
None adult View