Ignite Creation Date:
2025-12-25 @ 1:34 AM
Ignite Modification Date:
2026-02-06 @ 12:53 AM
Study NCT ID:
NCT03488394
Status:
ACTIVE_NOT_RECRUITING
Last Update Posted:
2025-12-09
First Post:
2018-03-22
Is Gene Therapy:
True
Has Adverse Events:
False
Brief Title:
Gene Therapy With Modified Autologous Hematopoietic Stem Cells for the Treatment of Patients With Mucopolysaccharidosis Type I, Hurler Variant
Sponsor:
Orchard Therapeutics
Organization: