Viewing StudyNCT00074919



Ignite Creation Date: 2024-05-05 @ 11:33 AM
Last Modification Date: 2024-10-26 @ 9:09 AM
Study NCT ID: NCT00074919
Status: APPROVED_FOR_MARKETING
Last Update Posted: 2014-02-05
First Post: 2003-12-23

Brief Title: Expanded Access Use of Myozyme Alglucosidase Alfa in Patients With Infantile-onset Pompe Disease
Sponsor: Genzyme a Sanofi Company
Organization: Sanofi

Conditions & Keywords Data

Conditions:
Name
Glycogenosis 2
Glycogen Storage Disease Type II
Keywords:
Name View
Acid Maltase Deficiency Disease View
Glycogen Storage Disease Type II View
GSD-II View
Pompe Disease View