Eligibility Module
The Eligibility Module contains detailed information about who can participate in the clinical trial. This includes eligibility criteria, age restrictions, gender requirements, healthy volunteer status, and study population descriptions, helping researchers understand who is eligible to participate in the study.
Eligibility Module path is as follows:
Study -> Protocol Section -> Eligibility Module
Eligibility Module
Ignite Creation Date:
2025-12-24 @ 4:56 PM
Ignite Modification Date:
2025-12-24 @ 4:56 PM
NCT ID:
NCT05994950
Eligibility Criteria:
Inclusion Criteria:
* Patient aged \<16 years old as of 1st July 2017. (16 years old is the age in which patients typically start their transition process to adulthood - retrospective data collection will stop at the date in which the patient turned 16 years old, if this is before 30th June 2022).
* OR patient was born between 1st July 2017 - 30th June 2022.
* Genetically confirmed 5q SMA.
* Patients must have been under the care of the named Key Collaborative Site and Neuromuscular Service for their SMA anytime during 1st July 2017- 30th June 2022 and must have had at least two clinical reviews during this time.
* Deceased patients can be reviewed, as long as they met the eligibility criteria before their date of death.
Exclusion Criteria:
* Aged ≥16 years as of 1st July 2017.
* Genetically confirmed as having non-5q SMA or have no genetic confirmation of their diagnosis.
* Patient was not under the care of the named Key Collaborative Site and Neuromuscular Service for their SMA specialist care anytime during 1st July 2017 - 30th June 2022.
Healthy Volunteers:
False
Sex:
ALL
Minimum Age:
0 Years
Maximum Age:
16 Years
Study:
NCT05994950
Study Brief:
Protocol Section:
NCT05994950